6.49 (-%)
As of Oct 31, 2024
Source:
We are a clinical-stage genetic medicine company pioneering genome editing and gene delivery platforms to address rare and serious diseases from infancy through adulthood. Our genome editing platform, GeneRide™, is a new approach to precise gene insertion harnessing a cell's natural deoxyribonucleic acid, or DNA, repair process potentially leading to durable therapeutic protein expression levels. Our gene delivery platform, sAAVy™, is an adeno-associated virus, or AAV, capsid engineering platform designed to optimize gene delivery for treatments in a broad range of indications and tissues.
Country | United States |
Headquarters | lexington, massachusetts |
Phone Number | 617-245-0399 |
Industry | manufacturing |
CEO | |
Website |